Anemia, Hemolytic, Congenital Nonspherocytic - 3 Studies Found
Active, not recruiting |
: Pyruvate Kinase Deficiency Natural History Study :
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Active, not recruiting |
: A Study of AG-348 in Adult Patients With Pyruvate Kinase Deficiency : Pyruvate Kinase Deficiency : 2015-06-10 : Drug: AG-348 A range of doses of AG-348 will be tested based on the assessment of safety, tolerability a |
Recruiting |
: Fat and Sugar Metabolism During Exercise in Patients With Metabolic Myopathy :
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