Limb-girdle Muscular Dystrophy, Type 2B - 5 Studies Found
Completed |
: Deflazacort in Dysferlinopathies :
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Active, not recruiting |
: Clinical Outcome Study for Dysferlinopathy :
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Completed |
: Evaluation of Limb-Girdle Muscular Dystrophy :
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Completed |
: The Safety and Biological Activity of ATYR1940 in Patients With Limb Girdle or Facioscapulohumeral Muscular Dystrophies :
: 2015-09-28 :
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Recruiting |
: rAAVrh74.MHCK7.DYSF.DV for Treatment of Dysferlinopathies : Dysferlinopathy : 2016-02-11 : Drug: rAAVrh74.MHCK7.DYSF.DV Biological/Vaccine: rAAVrh74.MHCK7.DYSF.DV Recombinant adeno-associated vir |