Search for Clinical Trial Results
Leukodystrophy - 153 Studies Found
Status | Study |
Recruiting |
Study Name: UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells Condition:
Interventions: |
Completed |
Study Name: Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation Condition:
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Recruiting |
Study Name: MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis Condition:
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Completed |
Study Name: Stem Cell Transplant for Inborn Errors of Metabolism Condition:
Interventions: |
Active, not recruiting |
Study Name: The Natural History of Metachromatic Leukodystrophy Condition: Metachromatic Leukodystrophy Date: 2008-03-11 |
Recruiting |
Study Name: Intracerebral Gene Therapy for Children With Early Onset Forms of Metachromatic Leukodystrophy Condition: Metachromatic Leukodystrophy Date: 2013-01-28 Interventions: Genetic: intracerebral administration of AAVrh.10cuARSA |
Completed |
Study Name: Multicenter Study of HGT-1110 Administered Intrathecally in Children With Metachromatic Leukodystrophy (MLD) Condition: Metachromatic Leukodystrophy (MLD) Date: 2011-12-14 Interventions: Biological: Recombinant human arylsulfatase A 6 patients treated with HGT-1110 EOW by IT injection |
Completed |
Study Name: Effect of Warfarin in the Treatment of Metachromatic Leukodystrophy Condition: Metachromatic Leukodystrophy Date: 2008-05-21 Interventions: Drug: Warfarin Oral administration (QD), variable dosage: patients will undergo blood test for PT/INR at |
Withdrawn |
Study Name: An Observational Study of Pediatric Subjects With Globoid Cell Leukodystrophy (GLD) Condition: Leukodystrophy, Globoid Cell Date: 2010-03-24 |