Barth Syndrome - 6 Studies Found
Completed |
: Exercise Training in Barth Syndrome : Barth Syndrome : 2010-08-30 : Behavioral: Exercise training aerobic exercise training, 45-60 minutes, 3x/week, 12 weeks (3-months) |
Recruiting |
: Heart and Muscle Metabolism in Barth Syndrome : Barth Syndrome : 2012-06-19 |
Recruiting |
: Resistance Exercise in Barth Syndrome : Barth Syndrome : 2012-06-20 : Behavioral: Resistance exercise and protein supplementation Resistance exercise training will occur 3x/w |
Recruiting |
: A Trial to Evaluate Safety, Tolerability and Efficacy of Elamipretide in Subjects With Barth Syndrome : Barth Syndrome : 2017-03-21 : Drug: Elamipretide 40 mg daily subcutaneous injection for 12 weeks |
Available |
: Compassionate Use of Triheptanoin (C7) for Inherited Disorders of Energy Metabolism :
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Recruiting |
: North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC) :
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